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Duchenne muscular dystrophy - Articles and news items

ataluren

NICE allows extra time for agreement on ataluren price

Industry news / 4 May 2016 / Victoria White, Digital Content Producer

NICE has allowed extra time for further discussions on access arrangements for PTC Therapeutics’ Translarna (ataluren) for Duchenne Muscular Dystrophy…

Duchenne-muscular-dystrophy

NICE recommends ataluren for Duchenne muscular dystrophy

Industry news / 18 April 2016 / Victoria White, Digital Content Producer

NICE has recommended Translarna (ataluren) for treating children aged 5 and over with Duchenne muscular dystrophy caused by a nonsense mutation…

drisapersen

BioMarin submits MAA for drisapersen for the treatment of Duchenne muscular dystrophy amenable to exon 51 skipping

Industry news / 8 June 2015 / Victoria White

BioMarin has submitted a MAA for drisapersen for the treatment of the largest subset of Duchenne muscular dystrophy (DMD) amenable to single exon skipping…

 

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