Paolo Galfetti

FDA grants Orphan Drug Designation to phenylketonuria treatment

A new treatment called APR-OD031 has been given Orphan Drug…

7 April 2020 | By Victoria Rees (European Pharmaceutical Review)

A new treatment called APR-OD031 has been given Orphan Drug Designation (ODD) by the FDA, for the treatment of phenylketonuria.

news

FDA grants Orphan Drug Designation to Epidermolysis Bullosa treatment

The US Food and Drug Administration has awarded APR-TD011 Orphan…

9 December 2019 | By Victoria Rees (European Pharmaceutical Review)

The US Food and Drug Administration has awarded APR-TD011 Orphan Drug Designation, for the treatment of a rare disease.

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Paolo Galfetti

FDA grants Orphan Drug Designation to phenylketonuria treatment

FDA grants Orphan Drug Designation to Epidermolysis Bullosa treatment