transthyretin (ATTR) amyloidosis with cardiomyopathy

CHMP meeting highlights – April 2025

28 April 2025 | By Catherine Eckford (European Pharmaceutical Review)

The Committee for Medicinal Products for Human Use (CHMP) recommended approval of a variety of new medicines, including several treatments for hereditary and rare conditions.

news

Regulatory-first for gene editing therapy

19 October 2023 | By Catherine Eckford (European Pharmaceutical Review)

The world’s first investigational in vivo CRISPR-based gene editing therapy cleared for late-stage clinical development is expected to enter Phase III in late 2023.

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