All metachromatic leukodystrophy (MLD) articles

  • shutterstock_1146016232
    News

    FDA approves innovative gene therapy for MLD

    2024-03-20T16:42:03Z

    Following US FDA approval of Lenmeldy™ (atidarsagene autotemcel) for early-onset metachromatic leukodystrophy (MLD), the US wholesale acquisition cost of the gene therapy has been set to $4.25 million.

  • Clinical Biotechnology Centre for cell and gene therapy manufacture
    News

    New NHS cell and gene therapy centre opens

    2023-03-10T12:04:47Z

    The new Clinical Biotechnology Centre (CBC) in Bristol will manufacture cell and gene therapies to help boost the UK life sciences sector.