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Alongside Phase III data demonstrating significant efficacy in the rare…
31 July 2025 | By Catherine Eckford (European Pharmaceutical Review)
Alongside Phase III data demonstrating significant efficacy in the rare disease, the FDA’s decision could position the small molecule as a future standard of care.
As part of the agreement with Novartis Pharmaceuticals, PTC will…
3 December 2024 | By Catherine Eckford (European Pharmaceutical Review)
As part of the agreement with Novartis Pharmaceuticals, PTC will receive an initial $1 billion to develop the potential first-in-class oral therapy.
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