dystrophic epidermolysis bullosa (DEB)

Year in review: EPR’s top stories of 2023

18 December 2023 | By Catherine Eckford (European Pharmaceutical Review)

EPR wraps up the year with a selection of top stories from 2023, highlighting key trends and topics such as environmental monitoring (EM), quality (QA/QC), manufacturing, regulation and clinical development.

news

First redosable gene therapy approved

24 May 2023 | By Catherine Eckford (European Pharmaceutical Review)

The “landmark approval” of a redosable gene therapy for dystrophic epidermolysis bullosa “ushers in a whole new paradigm to treat genetic diseases".

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dystrophic epidermolysis bullosa (DEB)

Year in review: EPR’s top stories of 2023

First redosable gene therapy approved