β-thalassemia

First CRISPR-based gene-editing therapy authorised

16 November 2023 | By Catherine Eckford (European Pharmaceutical Review)

The UK Medicines and Healthcare products Regulatory Agency (MHRA) has granted a world-first regulatory authorisation to a medicine based on Nobel Prize-winning technology.

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β-thalassemia

First CRISPR-based gene-editing therapy authorised