Adrenoleukodystrophy (ALD)

EMA’s human medicines committee (CHMP) meeting highlights, May 2021

24 May 2021 | By Hannah Balfour (European Pharmaceutical Review)

In its latest meeting the CHMP recommended eight medications for approval, 17 medicines for indication extension and concluded reviews of two COVID-19 treatments.

DNA double helix in blue with a specific region (gene) highlighted in yellow - idea of gene therapy

news

bluebird bio releases new data on its gene therapy for cerebral adrenoleukodystrophy

16 March 2021 | By Hannah Balfour (European Pharmaceutical Review)

Data from nearly seven years of follow up suggests one-time treatment with eli-cel may durably stabilise cerebral adrenoleukodystrophy disease progression.

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Adrenoleukodystrophy (ALD)

EMA’s human medicines committee (CHMP) meeting highlights, May 2021

bluebird bio releases new data on its gene therapy for cerebral adrenoleukodystrophy