Elfabrio (pegunigalsidase alfa)

NICE recommends new Fabry disease treatment

4 September 2023 | By Catherine Eckford (European Pharmaceutical Review)

Recommendation of Elfabrio® (pegunigalsidase alfa) means patients with Fabry disease in England will be able to access a new treatment option.

news

EMA’s human medicines committee (CHMP) meeting highlights – February 2023

2 March 2023 | By Catherine Eckford (European Pharmaceutical Review)

In its latest meeting, the Committee for Medicinal Products for Human Use (CHMP) recommended eight new medicines for approval, including an enzyme replacement therapy for a rare disease.

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Elfabrio (pegunigalsidase alfa)

NICE recommends new Fabry disease treatment

EMA’s human medicines committee (CHMP) meeting highlights – February 2023