Tegsedi (inotersen)

Various colours/sizes/shapes of pills and capsules laid out on a stack of 100 Euro notes

What impact does disease rarity have on rare and orphan drug pricing?

5 February 2021 | By Bhavesh Patel (CRA), Cécile Matthews (CRA), Owen Male (CRA)

Bhavesh Patel, Cécile Matthews and Owen Male at CRA’s Life Sciences Practice assess the relationship between drug pricing for rare disease therapies and disease prevalence in Europe, taking a closer look at payer assessments of orphan drugs in Germany.

news

EMA recommends marketing authorisation to Tegsedi for hereditary transthyretin amyloidosis

7 June 2018 | By European Pharmaceutical Review

The EMA has recommended granting a marketing authorisation for Tegsedi, a medicine for the treatment of stage 1 or stage 2 polyneuropathy...

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Recommended

Tegsedi (inotersen)

What impact does disease rarity have on rare and orphan drug pricing?

EMA recommends marketing authorisation to Tegsedi for hereditary transthyretin amyloidosis