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Roctavian (valoctocogene roxaparvovec)

First gene therapy approved for Haemophilia A

30 June 2023 | By Catherine Eckford (European Pharmaceutical Review)

The first approved gene therapy for haemophilia A reduced the mean annualised bleeding rate from 5.4 bleeds to 2.6 bleeds per year in a clinical study.

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EMA releases human medicines highlights 2022 report

17 February 2023 | By Catherine Eckford (European Pharmaceutical Review)

Medicines which represented significant progress in their therapeutic areas have been listed in the European Medicines Agency's Human Medicines Highlights 2022 report.

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Potential blockbuster drugs to watch in 2023

10 January 2023 | By Catherine Eckford (European Pharmaceutical Review)

Lecanemab for Alzheimer's and the first potential gene therapy primed for US launch for haemophilia A are two potential blockbuster Drugs to Watch™, says a 2023 report.

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Europe approves first gene therapy for treatment of haemophilia A

30 August 2022 | By Caroline Peachey (European Pharmaceutical Review)

European approval of BioMarin’s ROCTAVIAN (valoctocogene roxaparvovec) one-time gene therapy represents a breakthrough in the treatment of adults with severe haemophilia A.

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Recommended

Roctavian (valoctocogene roxaparvovec)

First gene therapy approved for Haemophilia A

EMA releases human medicines highlights 2022 report

Potential blockbuster drugs to watch in 2023

Europe approves first gene therapy for treatment of haemophilia A