The FDA has awarded 11 grants equating to about $25 million of funding to clinical trials for the development of rare disease treatments.
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Boston Children's Hospital
A New Drug Application has been submitted to the FDA for lonafarnib, the first-ever treatment for Progeria and Progeroid Laminopathies.
The FDA requires drugs to be tested on children after they have been approved for adults, however two thirds of these are not happening...