AADC deficiency

EMA’s human medicines committee (CHMP) May 2022 meeting highlights

23 May 2022 | By Sarah Wills (European Pharmaceutical Review)

The latest meeting saw EMA’s human medicines committee (CHMP) recommend the approval of nine new medicines, refuse two biosimilar medications and recommend extensions of therapeutic indication for six medicines.

news

New targeted gene therapy could reverse neurological diseases

14 July 2021 | By Anna Begley (European Pharmaceutical Review)

Researchers have developed a novel gene therapy that could help treat children with incurable genetic and neurodegenerative diseases.

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AADC deficiency

EMA’s human medicines committee (CHMP) May 2022 meeting highlights

New targeted gene therapy could reverse neurological diseases