Orkambi (lumacaftor/ivacaftor)

Various colours/sizes/shapes of pills and capsules laid out on a stack of 100 Euro notes

What impact does disease rarity have on rare and orphan drug pricing?

5 February 2021 | By Bhavesh Patel (CRA), Cécile Matthews (CRA), Owen Male (CRA)

Bhavesh Patel, Cécile Matthews and Owen Male at CRA’s Life Sciences Practice assess the relationship between drug pricing for rare disease therapies and disease prevalence in Europe, taking a closer look at payer assessments of orphan drugs in Germany.

human shape with lungs highlighted and alveoli cut away - idea of respiratory therapeutics

news

Vertex’s Kaftrio approved for use in Europe and made accessible on the NHS

26 August 2020 | By Hannah Balfour (European Pharmaceutical Review)

The European Commission and European Medicines Agency have approved the triple combination Kaftrio for use in certain cystic fibrosis patients, triggering the drug to be accessible on the UK’s National Health Service.

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Orkambi (lumacaftor/ivacaftor)

What impact does disease rarity have on rare and orphan drug pricing?

Vertex’s Kaftrio approved for use in Europe and made accessible on the NHS