Tofersen

CHMP meeting highlights: February 2024

26 February 2024 | By Catherine Eckford (European Pharmaceutical Review)

Ten new medicines, including a new oligonucleotide therapy for ALS, were recommended for approval at the Committee for Medicinal Products for Human Use (CHMP)’s recent meeting.

news

EMA accepts marketing application for ALS treatment

6 December 2022 | By Catherine Eckford (European Pharmaceutical Review)

The EMA has accepted the marketing authorisation application for tofersen, which could be the first treatment for a rare genetic cause of ALS.

EMA accepts marketing application for ALS treatment

news

Experimental motor neurone disease therapy shows promise

14 July 2020 | By Hannah Balfour (European Pharmaceutical Review)

Tofersen reduced expression of the SOD1 gene known to cause amyotrophic lateral sclerosis (ALS) and slowed clinical decline in the Phase I/II trial.

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Tofersen

CHMP meeting highlights: February 2024

EMA accepts marketing application for ALS treatment

Experimental motor neurone disease therapy shows promise