Leber Congenital Amaurosis

AAO 2023: intravitreal treatment shows benefit in geographic atrophy (GA)

Novel blindness gene therapy shows promise in first-in-human trial

20 April 2021 | By Hannah Balfour (European Pharmaceutical Review)

The lowest dose of the gene therapy was shown to be safe and somewhat improved vision in the first three patients treated in the trial.

DNA strands overlaid on test tubes - idea of developing CRISPR therapeutics

news

CRISPR therapies could be one of the most transformative in human history, says GlobalData

16 March 2021 | By Hannah Balfour (European Pharmaceutical Review)

Adam Pearson, Senior Oncology Analyst at GlobalData, comments on the development of CRISPR-based therapies and outlines potential opportunities and challenges in the space.

news

Gene therapy receives Champalimaud Vision Award

4 September 2018 | By European Pharmaceutical Review

The Champalimaud Vision Award has been awarded to research teams for the development of a gene therapy...

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Leber Congenital Amaurosis

Novel blindness gene therapy shows promise in first-in-human trial

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