Progeroid laminopathies

Stamp reading 'FDA APPROVED' next to a stack of blue and white capsules in blister packaging

FDA approves first treatment for rare paediatric genetic diseases

24 November 2020 | By Hannah Balfour (European Pharmaceutical Review)

Zokinvy (lonafarnib) capsules have been approved for the treatment of Hutchinson-Gilford progeria syndrome and certain progeroid laminopathies in patients over one year old.

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Progeroid laminopathies

FDA approves first treatment for rare paediatric genetic diseases