PRX–102 (pegunigalsidase alfa)

NICE recommends new Fabry disease treatment

4 September 2023 | By Catherine Eckford (European Pharmaceutical Review)

Recommendation of Elfabrio® (pegunigalsidase alfa) means patients with Fabry disease in England will be able to access a new treatment option.

news

Enzyme replacement therapy approved for Fabry disease

8 May 2023 | By Catherine Eckford (European Pharmaceutical Review)

The European Commission (EC) has given approval to the first PEGylated enzyme replacement therapy to treat Fabry disease.

news

CHMP recommends first pegylated enzyme for Fabry disease

27 February 2023 | By Catherine Eckford (European Pharmaceutical Review)

A PEGylated enzyme replacement therapy for Fabry disease has received recommendation for a marketing authorisation from the European Medicines Agency (EMA)'s human medicines committee.

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Recommended

PRX–102 (pegunigalsidase alfa)

NICE recommends new Fabry disease treatment

Enzyme replacement therapy approved for Fabry disease

CHMP recommends first pegylated enzyme for Fabry disease